Sialidosis 

We have identified low uM inhibitors in vitro as potential chaperones that are under preclinical assessment.

Klein JJ, Baker NC, Foil DH, Zorn KM, Urbina F, Puhl AC, Ekins S. Using Bibliometric Analysis and Machine Learning to Identify Compounds Binding to Sialidase-1. ACS Omega. 2021 Jan 20;6(4):3186-3193. doi: 10.1021/acsomega.0c05591. Erratum in: ACS Omega. 2021 Jun 08;6(24):16253. PMID: 33553934